BP
BioMarin (San Rafael, CA). 2024 revenue ~$2.5B. Rare disease leader. Voxzogo (vosoritide, achondroplasia). Roctavian (valoctocogene roxaparvovec, hemophilia A gene therapy). Naglazyme, Vimizim, Brineura.
@bmrn
BioMarin (San Rafael, CA). 2024 revenue ~$2.5B. Rare disease leader. Voxzogo (vosoritide, achondroplasia). Roctavian (valoctocogene roxaparvovec, hemophilia A gene therapy). Naglazyme, Vimizim, Brineura.