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Ionis Pharmaceuticals (Carlsbad, CA). 2024 revenue ~$1.0B. Antisense oligonucleotide (ASO) pioneer. Spinraza (nusinersen, mit Biogen). Tegsedi (inotersen). Wainua (eplontersen, 2025). GalNAc ASO platform.

12:54:06 AM · Jul 9, 2026
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